Enhanced liver regeneration via targeted mRNA delivery for partial in vivo reprogramming

preprint OA: closed
📄 Open PDF Full text JSON View at publisher

Abstract

Recent studies suggest that injury-induced dedifferentiation, which leads to the formation of ‘injury-responsive cells’, contributes significantly to tissue repair across various organs, including the liver. Utilizing Yamanaka factors (Oct4, Sox2, Klf4, and c-Myc: OSKM) for in vivo partial reprogramming generates ‘injury-responsive cells’ in the intestine, mirroring those derived from injury-induced dedifferentiation. Thus, the transgene induction of OSKM or viral delivery of Oct4, Sox2, and Klf4 shows promise in facilitating tissue regeneration in the intestine, liver, skeletal muscle, and retina. Herein, we demonstrated that transient OSKM induction produces two distinct liver progenitor-like cell populations. One of these populations resembles liver progenitor-like cells (LPLCs) generated by acute acetaminophen (APAP) injury without triggering immune responses. To explore in vivo reprogramming as a viable strategy for tissue regeneration, we employed lipid nanoparticles (LNP) carrying OSKM mRNA (OSKM mRNA-LNP) to stimulate LPLCs formation. Notably, the production of Sox9+ LPLCs, and OSKM-induced dedifferentiation, was closely correlated with successful tissue regeneration in the liver post APAP injury. Thus, the OSKM mRNA-LNP approach represents a promising therapeutic intervention for the repair of acute liver injuries.
Full text 1,432 characters · extracted from oa-doi-fallback · click to expand
Abstract Recent studies suggest that injury-induced dedifferentiation, which leads to the formation of ‘injury-responsive cells’, contributes significantly to tissue repair across various organs, including the liver. Utilizing Yamanaka factors (Oct4, Sox2, Klf4, and c-Myc: OSKM) for in vivo partial reprogramming generates ‘injury-responsive cells’ in the intestine, mirroring those derived from injury-induced dedifferentiation. Thus, the transgene induction of OSKM or viral delivery of Oct4, Sox2, and Klf4 shows promise in facilitating tissue regeneration in the intestine, liver, skeletal muscle, and retina. Herein, we demonstrated that transient OSKM induction produces two distinct liver progenitor-like cell populations. One of these populations resembles liver progenitor-like cells (LPLCs) generated by acute acetaminophen (APAP) injury without triggering immune responses. To explore in vivo reprogramming as a viable strategy for tissue regeneration, we employed lipid nanoparticles (LNP) carrying OSKM mRNA (OSKM mRNA-LNP) to stimulate LPLCs formation. Notably, the production of Sox9+ LPLCs, and OSKM-induced dedifferentiation, was closely correlated with successful tissue regeneration in the liver post APAP injury. Thus, the OSKM mRNA-LNP approach represents a promising therapeutic intervention for the repair of acute liver injuries. Competing Interest Statement The authors have declared no competing interest.

Text is read by the "Ask this paper" AI Q&A widget below. Extraction quality varies by source — PMC NXML preserves structure cleanly, OA-HTML may include some navigation residue, and OA-PDF can have broken hyphenation. The publisher copy (via DOI) is the canonical version.

My notes (saved in your browser only)

Ask this paper AI returns verbatim quotes from the full text · source: oa-doi-fallback

Answers must be backed by verbatim quotes from this paper's full text. Hallucinated quotes are dropped automatically; if no verbatim passage answers the question, we say so. How this works

Citation neighborhood (no data yet)

We don't have any in-corpus citations linked to this paper yet. This is a recent paper (2025) — citers typically take a year or two to land, and the OpenAlex reference graph may still be filling in.

Source provenance

europepmc
last seen: 2026-05-20T01:45:00.602351+00:00